68 PART 2 Examining Tools and Processes
analyze the kinds of data you’re likely to encounter in human research. Your
strategy is to apply them to a clinical trial design. In clinical trials, changes in
values of variables over time, and differences between treatments in crossover
studies are often analyzed by paired t tests and repeated-measures ANOVAs.
Differences between groups of participants in parallel studies are often analyzed
by unpaired t tests and ANOVAs. Often, final regression models are developed for
clinical trial interpretation because these can control for residual confounding
(which are covered in the chapters in Part 5). In longer clinical trials, time until
death (survival time) and the times to the occurrence of other endpoint events
(besides death) are analyzed by survival methods (Part 6 focuses on survival anal-
ysis methods).
Determining how many participants
to enroll in a clinical trial
Chapter 3 presents the concept of statistical power, and for a clinical trial, you
should enroll enough participants to provide sufficient statistical power when
testing the primary objective of the study. The specific way you calculate the
required sample size depends on the statistical test that’s used for the primary
hypothesis. Each chapter of this book that describes hypothesis tests also shows
how to estimate the required sample size for that test. To get quick sample-size
estimates, you can use G*Power (an application for sample-size calculations
described in Chapter 4), or you can use the formulas, tables, and charts in
Chapter 25 and on the book’s Cheat Sheet at www.dummies.com (just search for
“Biostatistics For Dummies Cheat Sheet”).
You must also allow some extra space in your target sample-size estimate for
some of the enrolled participants to drop out or otherwise not contribute the data
you need for your analysis. For example, suppose that you need full data from
64 participants for sufficient statistical power to answer your main objective. If
you expect a 15 percent attrition rate from the study, which means you expect only
85 percent of the enrolled participants to have analyzable data, then you need
to plan to enroll 64/0.84, or 76, participants in the study.
Assembling the study protocol
A study protocol (or just protocol) is a document that lays out exactly what you plan
to do to collect and analyze data in a research study. For ethical reasons, every
research study involving human participants should have a protocol, and for other
types of studies, having a protocol prepared before starting the research is